These trials completed more than 12 months ago and should have reported results.

These trials are not yet due to report results: some are ongoing, some completed within the past 12 months.

These trials have problematic data on the registry. Details why »

Status Trial ID Title Completion date Category
Exempt, with results 2010-024068-16 An open label multicenter study to evaluate the safety, tolerability and pharmacokinetics of SBC-102 in adult patients with liver dysfunction due to lysosomal acid lipase deficiency. 2012-01-06 not-yet-due
Reported results 2011-000032-28 An Open Label, Multicenter, Dose Escalation Study to Evaluate the Safety, Tolerability, Efficacy, Pharmacokinetics, and Pharmacodynamics of SBC-102 in Children with Growth Failure Due to Lysosomal Aci... 2018-01-03 due-trials
Reported results 2011-001513-13 AN OPEN LABEL MULTICENTER EXTENSION STUDY TO EVALUATE THE LONG-TERM SAFETY, TOLERABILITY, AND EFFICACY OF SBC-102 IN ADULT SUBJECTS WITH LIVER DYSFUNCTION DUE TO LYSOSOMAL ACID LIPASE DEFICIENCY WHO P... 2017-07-10 due-trials
Listed as ongoing, but also has a completion date and reported results 2011-002750-31 A multicenter, randomized, placebo-controlled study of SBC-102 in patients with lysosomal acid lipase deficiency 2018-12-11 bad-data
Listed as ongoing, but also has a completion date 2011-002880-42 An Open Label Multicenter Extension Study to Evaluate the Long-Term Efficacy and Safety of SBC 102 in Children with Lysosomal Acid Lipase Deficiency Who Previously Received Treatment with SBC-102 2012-11-30 bad-data
Listed as ongoing, but also has a completion date and reported results 2011-004287-30 A Multicenter, Open-Label Study of Sebelipase Alfa in Patients with Lysosomal Acid Lipase Deficiency 2017-12-28 bad-data
Listed as ongoing, but also has a completion date 2014-000533-22 A Phase 2, Open Label, Multicenter Study to Evaluate the Safety, Tolerability, Efficacy, and Pharmacokinetics of Sebelipase Alfa in Infants with Rapidly Progressive Lysosomal Acid Lipase Deficiency 2018-10-30 bad-data