These trials completed more than 12 months ago and should have reported results.

These trials are not yet due to report results: some are ongoing, some completed within the past 12 months.

These trials have problematic data on the registry. Details why »

Status Trial ID Title Completion date Category
Exempt, with results 2016-001446-25 AAV8-mediated Low Density Lipoprotein Receptor (LDLR) Gene Replacement in Subjects with Homozygous Familial Hypercholesterolemia (HoFH) 2020-11-27 not-yet-due
Ongoing 2019-004496-39 A Long-term Follow-up Study to Evaluate the Safety and Efficacy of RGX-501 Studio di follow-up a lungo termine per valutare la sicurezza e l'efficacia di RGX-501 not-yet-due